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Satellite Symposia
Participation in the satellite symposia is free of charge. We thank the companies for their programme contributions and support!
Tuesday, 3 Setember
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PTC THERAPEUTICS
Unlocking the potential of patients with AADC deficiency
Tuesday, 3 Setember 2024 | 12:45-13:45
Location:
Magnolia Auditorium | Level -1
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b60810f547f2e6cc8bb_SANOFI.jpg)
Sanofi
Transforming ASMD Management: Clinical Perspectives on Timely Diagnosis and Treatment of ASMD
Tuesday, 3 Setember 2024 | 12:45-13:45
Location:
Camellia Auditorium | Level 0
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b61794246ed615a3fd1_Takeda.png)
TAKEDA
Can we meet the challenges of living well with Fabry disease?
Tuesday, 3 Setember 2024 | 12:45-13:45
Location:
Laurel Room | Level -1
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b6211bee966e0dc5ac7_Ultragenyx.png)
ULTRAGENYX
A closer look at long-chain fatty acid oxidation disorders (LC-FAOD)
Tuesday, 3 Setember 2024 | 12:45-13:45
Location:
Plane Auditorium | Level 0
Wednesday, 4 Setember
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AMICUS THERAPEUTICS
Navigating multidisciplinary connections in Fabry disease: a patient centered approach from diagnosis to treatment
Wednesday, 4 Setember 2024 | 07:30-08:30
Location:
Camellia Auditorium | Level 0
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CHIESI GLOBAL RARE DISEASES
How to deal with uncertainty in LSDs to improvepatient care. The alpha-mannosidosis case
Wednesday, 4 Setember 2024 | 07:30-08:30
Location:
Plane Auditorium | Level 0
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66705fc3d2cb023480f059ad_iEcure_logo.png)
IECURE
Emerging Cell and Gene Therapy Approaches for OTC Deficiency
Wednesday, 4 Setember 2024 | 07:30-08:30
Room:
Laurel Room | Level -1
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/667028b35540da05b8cbe566_immedica%20pharma_get_company_logo.png)
ImMEDICA PHARMA
Meeting the Unmet Need: Introducing pegzilarginase for the treatment of Arginase 1 Deficiency
Wednesday, 4 Setember 2024 | 07:30-08:30
Location:
Magnolia Auditorium | Level -1
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b5d96b5f9f3ed76014e_BIOMARIN.jpg)
BIOMARIN
PKU management in evolution: Discussion on the changing soundscape
Wednesday, 4 Setember 2024 | 18:30-19:30
Room:
Camellia Auditorium | Level 0
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b60b8a4b4c1fc0f0bfc_Recordati.png)
Recordati
Optimising care of organic acidurias – Opportunities and challenges when treating patients long-term
Wednesday, 4 Setember 2024 | 18:30-19:30
Location:
Plane Auditorium | Level 0
Thursday, 5 Setember
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AMICUS THERAPEUTICS
Prioritizing Disease Monitoring in LOPD: Can We Do More?
Thursday, 5 Setember 2024 | 07:30-08:30
Location:
Camellia Auditorium | Level 0
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/667028b448873911da47d248_jnanatherapeutics-logo-fullcolor-rgb.png)
Jnana Therapeutics
Harnessing Hartnup as a potential treatment approach for PKU and related amino acid disorders
Thursday, 5 Setember 2024 | 07:30-08:30
Location:
Plane Auditorium | Level 0
MIRUM PHARMACEUTICS
Future Directions in the Diagnosis and Management of Inherited Metabolic Disorders Affecting Cholesterol Synthesis: Spotlight on CTX and SLOS
Thursday, 5 Setember 2024 | 07:30-08:30
Location:
Magnolia Auditorium | Level -1
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b5dbc4d52cefdb8f5e2_Chiesi.png)
CHIESI GLOBAL RARE DISEASES
Empowering voices in Fabry disease: collaborative advances intreatment and patient care
Thursday, 5 Setember 2024 | 12:30-13:30
Location:
Camellia Auditorium | Level 0
![](https://cdn.prod.website-files.com/648745b6eb46e9d6e98333d1/66548b60a10e63bc01d6791e_Orchard.png)
ORCHARD THERAPEUTICS
New Horizons for Metachromatic Leukodystrophy
with the advent of newborn screening
Thursday, 5 Setember 2024 | 12:30-13:30
Location:
Plane Auditorium | Level 0